Siblings raise funds for sialidosis gene therapy treatment

Two siblings from New Zealand, Faith Sinclair and Daniel Peach, are raising money for a gene therapy treatment in the U.S. They both have a rare genetic condition called sialidosis. This disorder has already claimed the life of their older brother, Antonn, who died at the age of 42. Sialidosis is an inherited metabolic disorder. It happens because of a faulty gene that stops cells from breaking down certain molecules. These molecules can build up in the body and cause serious health issues. Sinclair shared that there are only 55 known patients in the world with this condition. The siblings hope to undergo this groundbreaking therapy to improve their health. They have set up a fundraising page on Givealittle to gather the necessary funds for the treatment. They are determined to fight the disease that has affected their family.